Vyjuvek was approved in 2023, initially for patients at least six months of age, and could only be applied by healthcare professionals.

Investigators have used base editing to create a treatment for multisystemic smooth muscle dysfunction syndrome, which has ...

The firm's commercialization push is fueled by $35.6 million from a recent Series C financing and a $15.5 million ...

Funded through a $17 million NIH grant, the program will try six strategies to combat HIV and advance the most promising.

The selection committee picked Keytruda in certain biomarker-informed indications and the cystic fibrosis drug Trikafta.

The agency said it will accept data from single-arm trials in its newly released Rare Disease Evidence Principles, but ...

Autonomous AI tools have great potential in supporting precision medicine, but developers are still figuring out how to deploy them in patient care.

The firm will use the proceeds to fund clinical trials in thyroid eye disease, diabetes, geographic atrophy, and other chronic diseases.

Phase II/III data showed that advanced gastric cancer patients on anbenitamab and chemotherapy fared better than those on standard therapy.

Some feel the guidance may encourage consistent follow-up of overall survival after accelerated approvals, but others remain focused on speeding new drugs to patients.

The firm said it will enroll more ovarian cancer patients in its ongoing Phase II trial to gather data for a regulatory submission for rezatapopt to the FDA.

The company announced results from a Phase Ib trial of the drug as a first-line monotherapy for EGFR PACC-mutated NSCLC.