Caring for three sons with Duchenne MD means that all columnist Betty Vertin has left are the leftovers, but this week, even they ran out.

Agamree is as effective as traditional corticosteroids at preserving walking ability but carries a lower risk of side effects ...

Columnist Robin Stemple and others in the Western Pennsylvania chapter of the FSHD Society raised $85,000 for research toward ...

Sarepta said DMD treatments Amondys 45 and Vyondys 53 show 'positive and encouraging trends' even though a trial failed to ...

Dosing has begun in a long-term extension study testing Satellos Bioscience’s experimental oral therapy SAT-3247 in men with ...

In an effort to improve his heart health, columnist Shalom Lim trials a new medication for his cardiomyopathy, a complication ...

Whether it's transportation, education, or treatment, the more choices people with LGMD have, the better, says columnist.

Exon skipping is a treatment approach for people with Duchenne muscular dystrophy (DMD) that, while not a cure, may help to make the effects of the genetic disease less severe. Duchenne, the most ...

Columnist Betty Vertin shares how she explained Duchenne muscular dystrophy to her sons, who received their DMD diagnosis at a young age.

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

A young man with Duchenne muscular dystrophy (DMD) who received the one-time gene therapy Elevidys (delandistrogene moxeparvovec-rokl) has died due to acute liver failure. In a statement, the ...

Doctors can use several tests to diagnose muscular dystrophy (MD). A correct diagnosis gives patients an understanding of how their disease is likely to progress. It also helps doctors do a better job ...