资讯

Back to School Without the Math Meltdowns Back to school should feel like popping champagne—not hiding in the pantry with a ...
编者按:近年来,寡核苷酸类药物凭借其直接调控基因表达的独特机制,在中枢神经系统(CNS)疾病治疗领域展现出巨大潜力,受到业内广泛关注。迄今为止,美国FDA已批准多款寡核苷酸药物用于CNS疾病的治疗,如脊髓性肌萎缩症(SMA)和肌萎缩侧索硬化症(ALS ...