ATTR-PN diagnosis requires a combination of neurological and non-neurological tests, such as blood pressure monitoring, a ...

Overall, the life expectancy of patients with SCD is lower than that of persons without SCD. 1 However, life expectancy varies depending on the type of disease, treatments administered, and ...

The most important goal of patients with generalized myasthenia gravis and their caregivers was to achieve stable disease. Patients with generalized myasthenia gravis (gMG) still have many unmet needs ...

Patients treated with combined low-dose rituximab regimen had better improvements and a higher proportion of favorable response in scale assessments at each follow-up visit. A simplified regimen of ...

There was no statistically significant association between the concentration of vatiquinone and Fridericia corrected QT interval. A supratherapeutic dose of 1400 mg of vatiquinone is safe and ...

This case report corresponds with others suggesting that tobacco use and asbestos exposure may be associated with the pathophysiology of IgG4-RD. An elderly male patient with a history of smoking and ...

Living with Pompe disease is a constant battle requiring physical resilience and emotional strength. And it requires the ability to adapt to a life that progressively becomes more challenging. Yet, ...

Test Your Knowledge About the Signs and Symptoms of ITP Test Your Knowledge About the Types of ITP Test Your Knowledge About the Epidemiology of ITP ...

Investigators found that prior to the exchange transfusion procedure, neonates with ABO blood group incompatibility had higher levels of serum total bilirubin and serum indirect bilirubin, and higher ...

As of November 2024, approximately 156 clinical trials for Duchenne muscular dystrophy (DMD) are ongoing or pending: 16 trials not yet recruiting, 65 currently recruiting, 28 trials that are active ...

Chronic lymphocytic leukemia (CLL) is a hematologic malignancy characterized by the clonal expansion of abnormal B lymphocytes. 1 Despite significant advancements in targeted therapies like Bruton’s ...