Combining a premade SMN protein with a Spinraza-like drug (targets SMN2 gene) helped patient-derived motor neurons; potential ...

The Phase 3 STEER trial enrolled more than 100 children with SMA type 2, ages 2-17, who were able to sit, but hadn't walked ...

It's been a hard year for columnist Brianna Albers, but hard times make good times better. She's decided to focus on gratitude.

The top 10 most-read stories published by SMA News Today in 2024 focused on symptoms, treatments, and diagnosis.

An algorithm that takes into account clinical measures of motor symptom severity alongside data on factors like age and height may help predict the risk of scoliosis in people with spinal muscular ...

Edward Smith, MD, is an adjunct professor of pediatrics at Duke University Hospital. He earned his medical degree from the University of Mississippi School of Medicine and has practiced since 2007. He ...

SMA Europe is launching an initiative to share personal stories of how treatment affects the lives of people with spinal muscular atrophy (SMA). The initiative comes as part of OdySMA, an SMA Europe ...