OF THE MANY patients who need an organ from a donor, 90% go without. About 240m people live with rare genetic diseases, most of which cannot be treated. Each year poor diets cause more than 10m early ...

Instead of pulling cells out of the body, editing them, and putting them back in, scientists have now found a way to send CRISPR tools directly to specific cells inside living animals. By wrapping ...

The practice of genetic modification is as old as humanity. For thousands of years, humans have bred crops, livestock and even pets that possess desirable traits. This selective process, which alters ...

Nearly 80% of patients with a rare inherited blindness regained some vision after CRISPR-based gene editing. From recognizing lights on a coffee machine to navigating obstacles, these improvements ...

Banas is associate director of research at the Gene Editing Institute at ChristianaCare, where Kmiec is founder and executive director. The medical promise of CRISPR gene editing can be seen most ...

First-mover advantages are a big deal in the world of pharmaceuticals. CRISPR Therapeutics scored the first-ever regulatory approval for a CRISPR/Cas9 treatment this month. While logistical challenges ...

Transthyretin amyloidosis with cardiomyopathy (ATTR-CM) is a progressive, often fatal disease. Nexiguran ziclumeran (nex-z) is an investigational therapy based on CRISPR-Cas9 (clustered regularly ...

CRISPR gene editing is a genetic technique that removes mutated genes and replaces them with nonmutated ones. While some research indicates it may help with vision, there is no conclusive evidence.

The world's first patient to be treated with personalized gene editing therapy is finally headed home after over 300 days in the hospital. Nine-month-old KJ Muldoon recently underwent CRISPR-based ...